News
Research Video Series – Interruptions are Encouraged
January 9, 2025
GENERATION-HD2 Completed Recruitment
December 23, 2024
uniQure Update on FDA Discussions
December 10, 2024
NEW Video – Blue Skies for Skyhawk
December 6, 2024
NEW Research Video – Mini Brains
November 25, 2024
Difficult News – Sage Therapeutics DIMENSION STUDY
November 20, 2024
Update from Wave
November 12, 2024
An Update from Spark
November 8, 2024
October HDYO Survey Series Update
November 5, 2024
Breaking Down Barriers – A Conversation Around Access
October 23, 2024