News
PTC518 PIVOT-HD Study Achieves Primary Endpoint
May 5, 2025
An Update from Prlienia
April 28, 2025
An Update on Dosing for GENERATION HD2
April 17, 2025
uniQure Announces FDA Breakthrough Therapy Designation
April 17, 2025
Breaking Down Barriers – The Impact of Huntington’s Disease on Young People
April 7, 2025
NEW Research Video – Spotting HD Early
March 25, 2025
HDYO Mid-Strategy Report
March 5, 2025
A Helpful Template to Guide You in Submitting Your Public Response to CMS
February 6, 2025
Breaking Down Barriers – HD Young Adult Study
January 21, 2025
HD-YAS Study – Early Disease Progression
January 16, 2025