News
uniQure Announces Successful UK MHRA Pre-Submission Meeting for AMT-130 in Huntington’s Disease
May 6, 2026
Votoplam data from long-term extension study (Phase 2 LTE)
April 28, 2026
Novartis’ INVEST-HD Phase 3 trial: Site Initiations in USA and Canada
March 17, 2026
Breaking Down Barriers – Observational Studies’ Impact on Trials & Questions About Placebos
March 17, 2026
uniQure Provides Regulatory Update
March 2, 2026
Harness Therapeutics Nominates HRN001
February 16, 2026
Novartis Announces INVEST-HD
February 9, 2026
Research Video Series: Sertraline May Lighten the Load
February 5, 2026
Sarepta Receives Approval of Clinical Trial Application
February 4, 2026
An Update on SKY-0515
January 26, 2026