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Research Video Series – uniQure Update on Gene Therapy

August 25, 2022

Huntington's Disease Youth Organization

For more information about HDYO visit our website

www.hdyo.org

The Research Video Series was developed to break down HD Buzz's articles even further. This month's edition focuses on the recent article: uniQure Update on Gene Therapy. This video showcases the article's highlights.

uniQure is conducting safety trials of the first gene therapy for HD. A recent press release provided a 1 year update on the first group of 10 people who underwent surgery to receive this experimental drug. Complete article at https://en.hdbuzz.net/327.

Recently, uniQure also announced the postponement of AMT-130 higher-dose procedures due to recent suspected unexpected severe adverse reactions at this dose; Lower-dose procedures have not been affected. Read Community Letter under news at https://en.hdyo.org/a/725-uniqure-update.

HDYO's Research Video Series is sponsored by: Sage Therapeutics, Neurocrine Biosciences, uniQure and Teva Pharmaceutical Industries Ltd.

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