The US family and patient advocacy organizations are collaborating for key messaging on important initiatives, including asks to the FDA. HDSA, Help4HD, HD Reach, HDF and HDYO have all endorsed a petition directly to the FDA with the below concerns. Huntington’s Disease Can’t Wait!
The Time is NOW! Join the Fight to Bring Hope to HD Families: Urge the FDA to Uphold Accelerated Approval!
Sign the Petition Today Don’t forget to confirm your email to make it count.
Key Asks of the FDA:
➡️ Honor Your Previous Guidance: Fully uphold the previously agreed-upon accelerated approval pathway for AMT-130, including the use of external control data from natural history studies.
➡️ Recognize the Urgency: Acknowledge the dire, unmet medical need in the HD community and act with the expediency that Breakthrough Therapy and RMAT designations demand.
➡️Expedite Review: Make the review and approval of AMT-130, and any other future HD therapies, a top priority to get this potentially life-altering therapy to patients without further delay.
